Prednisone and deflazacort in Duchenne muscular dystrophy: a patient perspective and plain language summary publication of the Cincinnati study

20 Jun 2022

Written by Olivia Seifert, Editor

Comparative effectiveness research Journal articles Rare diseases and orphan drugs Real-world evidence Rheumatology

Wong B, Cook T, Miller H | Journal of Comparative Effectiveness Research, 11(11) (ePub ahead of print) (2022) Keywords: deflazacort • Duchenne muscular dystrophy • prednisone • real-world data Over in our sister journal, the Journal of Comparative Effectiveness Research, a plain language summary has been published covering the Cincinnati study, a research study previously published in the journal in January 2020. The Cincinnati study reviewed data from 435 males with Duchenne muscular dystrophy (DMD) who were treated at the Cincinnati Children's Hospital Medical Center (OH, USA). DMD is a rare disease that worsens over time. DMD patients experience inflammation...