How registries are learning and changing: a perspective from the EBMT Registry – Sofie Terwel

Return to the Spotlight: rare diseases and innovative therapies programme Learning objectives  Outline the 3 pillars of the EBMT and the main functions of its international registry Study the EBMT’s experience with CAR T-cell therapies as an example of how real-world data can be utilized to support regulatory decision-making Extrapolate the lessons learned from the example of CAR T-cell therapies Speaker biography Sofie Terwel works for the EBMT (London, UK), a non-profit organization in the field of hematological stem cell transplantation and cellular therapies. As project coordinator of the GoCART Coalition, she is responsible for the set-up and management of this multi-stakeholder initiative in the field of CAR T-cell therapies for hematological disease. Her aim is...